LITERATURE · PEER REVIEWED

Ash1l loss-of-function results in structural birth defects and altered cortical development

Brain · 2025 · Peer reviewed

COMPLETE CITATION

Citation and identifiers

Toolan KP, McGrath BT, Brinkmeier ML, et al.. “Ash1l loss-of-function results in structural birth defects and altered cortical development.” Brain. 148(1):55–68 · doi:10.1093/brain/awae218.

PubMed ID
38943682

RESEARCH QUESTION

How does Ash1l loss affect structural development, cortical progenitor balance, and neuronal fate in the tested mouse models?

Germline and cortical-lineage mouse perturbations produced structural birth defects and altered cortical development, findings that do not directly predict outcomes in human heterozygous disorder.

INTERPRETATION BOUNDARY

Read the finding and limit together.

What this study supports

Germline and cortical-lineage mouse models show structural birth defects, altered progenitor balance, and cortical-neuron-fate effects.

What it cannot establish

Developmental mouse findings, including homozygous outcomes, do not predict the course of human heterozygous ASH1L-related disorder.

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